40 studies found for:
"purine nucleoside phosphorylase deficiency" OR "Severe Combined Immunodeficiency"
Rank | Status | Study | ||||
---|---|---|---|---|---|---|
1 | Completed |
Transplantation of Hematopoietic Cells in Children With Severe Combined Immunodeficiency Syndrome
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2 | Recruiting |
Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID)
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3 | Recruiting |
Gene Therapy for X-linked Severe Combined Immunodeficiency
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4 | Completed |
Treatment for Growth Failure in Patients With X-Linked Severe Combined Immunodeficiency: Phase 2 Study of Insulin-Like Growth Factor-1
|
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5 | Completed |
Stem Cell Gene Therapy to Treat X-Linked Severe Combined Immunodeficiency (XSCID)
|
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6 | Active, not recruiting |
Total-Body Irradiation Followed By Cyclosporine and Mycophenolate Mofetil in Treating Patients With Severe Combined Immunodeficiency Undergoing Donor Bone Marrow Transplant
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7 | Active, not recruiting |
MND-ADA Transduction of CD34+ Cells From Children With Adenosine Deaminase (ADA)-Deficient Severe Combined Immunodeficiency (SCID)
|
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8 | Recruiting |
Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants
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9 | Recruiting |
Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral Vector
|
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10 | Completed |
Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study
|
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11 | Recruiting |
Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1)
|
||||
12 | Completed |
Newborn Screening for Severe Combined Immunodeficiency (SCID) in a High-Risk Population
|
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13 | Completed |
Influences on Female Adolescents' Decisions Regarding Testing for Carrier Status of XSCID
|
||||
14 | Active, not recruiting |
Hematopoietic Stem Cell Transplantation (HSCT) for Children With SCID Utilizing Alemtuzumab, Plerixafor & Filgrastim
|
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15 | Terminated |
Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies
|
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16 | Recruiting |
Establishing Fibroblast-Derived Cell Lines From Skin Biopsies of Patients With Immunodeficiency or Immunodysregulation Disorders
|
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17 | Recruiting |
Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency
|
||||
18 | Completed |
Cord Blood Stem Cell Transplantation Study (COBLT)
|
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19 | Recruiting |
Use of G-CSF to Obtain Blood Cell Precursors
|
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20 | Not yet recruiting |
EZN-2279 in Patients With ADA-SCID
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† Indicates status has not been verified in more than two years