List of Compassionate Allowances Conditions

A B C D E F G H I J K L M N O P Q R S T U V W X Y Z

Note: Conditions highlighted in Red are effective August 11, 2012.


1	Acute Leukemia
2	Adrenal Cancer - with distant metastases or inoperable, unresectable or recurrent
3	Aicardi-Goutieres Syndrome
4	Alexander Disease (ALX) - Neonatal and Infantile
5	Alobar Holoprosencephaly
6	Alpers Disease
7	Alpha Mannosidosis - Type II and III
8	Alstrom Syndrome
9	Amegakaryocytic Thrombocytopenia
10	Amyotrophic Lateral Sclerosis (ALS)
11	Anaplastic Adrenal Cancer - with distant metastases or inoperable, unresectable or recurrent
12	Angelman Syndrome
13	Aortic Atresia
14	Astrocytoma - Grade III and IV
15	Ataxia Telangiectasia
16	Batten Disease
17	Bilateral Retinoblastoma
18	Bladder Cancer - with distant metastases or inoperable or unresectable
19	Breast Cancer - with distant metastases or inoperable or unresectable
20	Canavan Disease (CD)
21	Carcinoma of Unknown Primary Site
22	Cerebro Oculo Facio Skeletal (COFS) Syndrome
23	Cerebrotendinous Xanthomatosis
24	Child Neuroblastoma - with distant metastases or recurrent
25	Child Non-Hodgkin Lymphoma - recurrent
26	Chondrosarcoma - with multimodal therapy
27	Chronic Myelogenous Leukemia (CML) - Blast Phase
28	Cornelia de Lange Syndrome-Classic Form
29	Corticobasal Degeneration
30	Creutzfeldt-Jakob Disease (CJD) - Adult
31	Cri du Chat Syndrome
32	Degos Disease, Systemic
33	Early-Onset Alzheimer’s Disease
34	Edwards Syndrome (Trisomy 18)
35	Eisenmenger Syndrome
36	Endomyocardial Fibrosis
37	Ependymoblastoma (Child Brain Tumor)
38	Esophageal Cancer
39	Ewing Sarcoma
40	Farber's Disease (FD) - Infantile
41	Fibrodysplasia Ossificans Progressiva
42	Follicular Dendritic Cell Sarcoma - metastatic or recurrent
43	Friedreichs Ataxia (FRDA)
44	Frontotemporal Dementia (FTD), Picks Disease -Type A - Adult
45	Fucosidosis - Type 1
46	Fukuyama Congenital Muscular Dystrophy
47	Galactosialidosis - Early and Late Infantile Types
48	Gallbladder Cancer
49	Gaucher Disease (GD) - Type 2
50	Glioblastoma Multiforme (Adult Brain Tumor)
51	Glioma Grade III and IV
52	Glutaric Acidemia - Type II
53	Head and Neck Cancers - with distant metastasis or inoperable or unresectable
54	Heart Transplant Graft Failure
55	Heart Transplant Wait List, 1A/1B
56	Hemophagocytic Lymphohistiocytosis (HLH), Familial Type
57	Hepatoblastoma
58	Histiocytosis Syndromes
59	Hutchinson-Gilford Progeria Syndrome
60	Hydranencephaly
61	Hypocomplementemic Urticarial Vasculitis Syndrome
62	Hypophosphatasia Perinatal (Lethal) and Infantile Onset Types
63	Hypoplastic Left Heart Syndrome
64	I Cell disease
65	Idiopathic Pulmonary Fibrosis
66	Infantile Free Sialic Acid Storage Disease
67	Infantile Neuroaxonal Dystrophy (INAD)
68	Infantile Neuronal Ceroid Lipofuscinoses
69	Inflammatory Breast Cancer (IBC)
70	Junctional Epidermolysis Bullosa, Lethal Type
71	Juvenile Onset Huntington Disease
72	Kidney Cancer - inoperable or unresectable
73	Krabbe Disease (KD) - Infantile
74	Kufs Disease Type A and B
75	Large Intestine Cancer - with distant metastasis or inoperable, unresectable or recurrent
76	Late Infantile Neuronal Ceroid Lipofuscinoses
77	Left Ventricular Assist Device (LVAD) Recipient
78	Leigh’s Disease
79	Lesch-Nyhan Syndrome (LNS)
80	Lewy Body Dementia
81	Lissencephaly
82	Liver Cancer
83	Lowe Syndrome
84	Lymphomatoid Granulomatosis - Grade III
85	Malignant Brain Stem Gliomas - Childhood
86	Malignant Melanoma - with metastases
87	Malignant Multiple Sclerosis
88	Mantle Cell Lymphoma (MCL)
89	Maple Syrup Urine Disease
90	Mastocytosis Type IV
91	Medulloblastoma - with metastases
92	Merkel Cell Carcinoma - with metastases
93	Merosin Deficient Congenital Muscular Dystrophy
94	Metachromatic Leukodystrophy (MLD) - Late Infantile
95	Mitral Valve Atresia
96	Mixed Dementias
97	MPS I, formerly known as Hurler Syndrome
98	MPS II, formerly known as Hunter Syndrome
99	MPS III, formerly known as Sanfilippo Syndrome
100	Mucosal Malignant Melanoma
101	Multicentric Castleman Disease
102	Multiple System Atrophy
103	Myoclonic Epilepsy with Ragged Red Fibers Syndrome
104	Neonatal Adrenoleukodystrophy
105	Nephrogenic Systemic Fibrosis
106	Neurodegeneration with Brain Iron Accumulation - Type 1 and Type 2
107	Niemann-Pick Disease (NPD) - Type A
108	Niemann-Pick Disease-Type C
109	Non-Small Cell Lung Cancer - with metastases to or beyond the hilar nodes or inoperable, unresectable or recurrent
110	Obliterative Bronchiolitis
111	Ohtahara Syndrome
112	Ornithine Transcarbamylase (OTC) Deficiency
113	Orthochromatic Leukodystrophy with Pigmented Glia
114	Osteogenesis Imperfecta (OI) - Type II
115	Osteosarcoma, formerly known as Bone Cancer - with distant metastases or inoperable or unresectable
116	Ovarian Cancer - with distant metastases or inoperable or unresectable
117	Pancreatic Cancer
118	Paraneoplastic Pemphigus
119	Patau Syndrome (Trisomy 13)
120	Pearson Syndrome
121	Pelizaeus-Merzbacher Disease-Classic Form
122	Pelizaeus-Merzbacher Disease-Connatal Form
123	Peripheral Nerve Cancer - metastatic or recurrent
124	Peritoneal Mesothelioma
125	Perry Syndrome
126	Pleural Mesothelioma
127	Pompe Disease - Infantile
128	Primary Cardiac Amyloidosis
129	Primary Central Nervous System Lymphoma
130	Primary Effusion Lymphoma
131	Primary Progressive Aphasia
132	Progressive Multifocal Leukoencephalopathy
133	Progressive Supranuclear Palsy
134	Pulmonary Atresia
135	Pulmonary Kaposi Sarcoma
136	Rett (RTT) Syndrome
137	Rhabdomyosarcoma
138	Rhizomelic Chondrodysplasia Punctata
139	Salivary Tumors
140	Sandhoff Disease
141	Schindler Disease Type 1
142	Single Ventricle
143	Small Cell Cancer (of the Large Intestine, Ovary, Prostate, or Uterus)
144	Small Cell Lung Cancer
145	Small Intestine Cancer - with distant metastases or inoperable, unresectable or recurrent
146	Smith Lemli Opitz Syndrome
147	Spinal Muscular Atrophy (SMA) - Types 0 And 1
148	Spinal Nerve Root Cancer-metastatic or recurrent
149	Spinocerebellar Ataxia
150	Stiff Person Syndrome
151	Stomach Cancer - with distant metastases or inoperable, unresectable or recurrent
152	Subacute Sclerosing Panencephalitis
153	Tabes Dorsalis
154	Tay Sachs Disease - Infantile Type
155	Thanatophoric Dysplasia, Type 1
156	The ALS/Parkinsonism Dementia Complex
157	Thyroid Cancer
158	Tricuspid Atresia
159	Ullrich Congenital Muscular Dystrophy
160	Ureter Cancer - with distant metastases or inoperable, unresectable or recurrent
161	Walker Warburg Syndrome
162	Wolf-Hirschhorn Syndrome
163	Wolman Disease
164	Xeroderma Pigmentosum
165	Zellweger Syndrome


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