36 studies found for:
Leukodystrophy
Rank | Status | Study | ||||
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1 | Recruiting |
Biomarker for Metachromatic Leukodystrophy Disease
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2 | Recruiting |
Imaging Study of the White Matter Lesions in Children With Metachromatic Leucodystrophy
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3 | Withdrawn |
An Observational Study of Pediatric Subjects With Globoid Cell Leukodystrophy (GLD)
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4 | Enrolling by invitation |
The Natural History of Infantile Globoid Cell Leukodystrophy
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5 | Recruiting |
Gene Therapy for Metachromatic Leukodystrophy
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6 | Recruiting |
Multicenter Study of HGT-1110, Enzyme Replacement Therapy Administered Intrathecally, in Children With Metachromatic Leukodystrophy (MLD)
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7 | Recruiting |
The Nosology and Etiology of Leukodystrophies of Unknown Causes
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8 | Not yet recruiting |
The Natural History of Metachromatic Leukodystrophy
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9 | Completed |
Effect of Warfarin in the Treatment of Metachromatic Leukodystrophy
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10 |
Completed
Has Results |
Long-term Metazym Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD)
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11 | Suspended |
HSCT for High Risk Inherited Inborn Errors
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12 | Completed |
The Classification and Cause of Leukodystrophies of Unknown Cause
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13 | Completed |
Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation
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14 | Completed |
Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD)
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15 | Terminated |
Open-Label Extension Study of Recombinant Human Arylsulfatase A (HGT-1111) in Late Infantile MLD
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16 | Unknown † |
Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation
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17 | Active, not recruiting |
Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders
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18 | Completed |
Stem Cell Transplantation (SCT) for Genetic Diseases
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19 |
Completed
Has Results |
Stem Cell Transplant for Inborn Errors of Metabolism
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20 | Suspended |
Lithium and Acetate for Canavan Disease
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† Indicates status has not been verified in more than two years