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Found 228 studies with search of: "Hemoglobinopathies"
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Rank Status Study
1 Active, not recruiting Allogeneic Stem Cell Transplantation Following Chemotherapy in Patients With Hemoglobinopathies
Conditions: Hemoglobinopathies;   Sickle Cell Disease;   Thalassemia
Interventions: Drug: Busulfex;   Drug: Fludarabine;   Drug: Alemtuzumab;   Procedure: Stem Cell Transfusion
2 Recruiting A Pilot Study of HSCT for Patients With High-Risk Hemoglobinopathy Using a Nonmyeloablative Preparative Regimen
Conditions: Sickle Cell Disease;   Thalassemia;   Hemoglobinopathies
Intervention: Drug: Busulfan; Fludarabine; cyclosporine A and MMF
3 Recruiting Interferon and Ribavirin Treatment in Patients With Hemoglobinopathies
Condition: Hemoglobinopathies
Intervention: Drug: PEG-IFN alpha2a or PEG-IFN alpha2b and Ribavirin
4 Terminated Bone Marrow Transplant From Related Donor for Patients With High Risk Hemoglobinopathies
Conditions: Sickle Cell Anemia;   Hemoglobinopathy;   Thalassemia
Interventions: Drug: Campath -1H;   Drug: Dilantin;   Drug: Busulfan;   Drug: Cyclophosphamide
5 Terminated Bone Marrow Transplant From Donor Using Less Toxic Conditioning for Patient With High Risk Hemoglobinopathies
Conditions: Sickle Cell Anemia;   Hemoglobinopathy;   Thalassemia
Interventions: Drug: FLUDARABINE;   Drug: CAMPATH-IH;   Procedure: Total Body Irradiation;   Drug: FK506;   Drug: G-SCF (Granulocyte-colony stimulating factor)
6 Active, not recruiting Stem Cell Transplantation After Reduced-Dose Chemotherapy for Patients With Sickle Cell Disease or Thalassemia
Conditions: Hemoglobinopathies;   Anemia, Sickle Cell;   Hemoglobin SC Disease;   Thalassemia;   Thalassemia Major
Interventions: Drug: Busulfex;   Drug: Fludarabine;   Drug: FK506;   Drug: Prednisone
7 Recruiting Magnetic Resonance Imaging (MRI) Assessments of the Heart and Liver Iron Load in Patients With Transfusion Induced Iron Overload
Conditions: Haemoglobinopathies;   Myelodysplastic Syndromes;   Post Bone Marrow Transplantation;   Transfusional Iron Overload
Intervention: Drug: deferasirox
8 Recruiting Reduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant Disorders
Conditions: Non Malignant Disorders;   Immunodeficiencies;   Congenital Marrow Failures;   Hemoglobinopathies;   Inborn Errors of Metabolism
Intervention: Other: Unrelated Umbilical Cord Blood Transplant
9 Completed Pediatric Hydroxyurea in Sickle Cell Anemia (PED HUG)
Conditions: Anemia, Sickle Cell;   Hematologic Diseases;   Hemoglobinopathies
Intervention: Drug: hydroxyurea
10 Recruiting Clinical and Laboratory Investigation of Humans With Informative Iron or Erythroid Phenotypes
Conditions: Hemoglobinopathies;   Hemolysis;   Iron Deficiency and Overload;   Anemias
Intervention:
11 Completed Penicillin Prophylaxis in Sickle Cell Disease (PROPS)
Conditions: Anemia, Sickle Cell;   Hematologic Diseases;   Hemoglobinopathies;   Infection (S. Pneumoniae);   Pneumonia
Intervention: Drug: penicillin
12 Completed Multicenter Study of Hydroxyurea in Patients With Sickle Cell Anemia (MSH)
Conditions: Anemia, Sickle Cell;   Hematologic Diseases;   Hemoglobinopathies
Intervention: Drug: hydroxyurea
13 Completed Chelation Therapy of Iron Overload With Pyridoxal Isonicotinoyl Hydrazone
Conditions: Anemia (Iron-Loading);   Beta-Thalassemia;   Hematologic Diseases;   Hemoglobinopathies;   Thalassemia;   Iron Overload
Intervention: Drug: chelation therapy
14 Completed Stroke Prevention in Sickle Cell Anemia (STOP 1)
Conditions: Anemia, Sickle Cell;   Cerebral Embolism and Thrombosis;   Cerebrovascular Disorders;   Hematologic Diseases;   Hemoglobinopathies
Intervention: Procedure: blood transfusion
15 Completed Evaluation of Subcutaneous Desferrioxamine as Treatment for Transfusional Hemochromatosis
Conditions: Anemia (Iron-Loading);   Beta-Thalassemia;   Hematologic Diseases;   Hemoglobinopathies;   Thalassemia;   Iron Overload;   Hemochromatosis
Intervention: Drug: deferoxamine
16 Recruiting Stem Cell Transplant for Hemoglobinopathy
Conditions: Sickle Cell Disease;   Thalassemia;   Severe Congenital Neutropenia;   Diamond-Blackfan Anemia;   Shwachman-Diamond Syndrome
Interventions: Drug: Cyclophosphamide, Fludarabine, Campath;   Drug: Busulfan, Cyclophosphamide, ATG
17 Completed Invasive Infections in Children With Hemoglobinopathies
Conditions: Thalassemia;   Sickle Cell Anemia
Intervention: Procedure: Historical records
18 Recruiting Allogeneic Bone Marrow Transplantation From HLA Identical Related Donors for Patients With Hemoglobinopathies
Conditions: Sickle Cell Disease;   HEMOGLOBIN SS;   HEMOGLOBIN SC;   Hemoglobin Sb0/+
Interventions: Procedure: ALLOGENEIC BMT/SCT Infusion;   Drug: Busulfan;   Biological: Campath 1H;   Drug: Cyclophosphamide and Mesna
19 Completed Hydroxyurea to Treat Beta-Thalassemia (Cooley's Anemia)
Conditions: Beta Thalassemia;   Hemoglobinopathy
Intervention: Drug: Hydroxyurea
20 Not yet recruiting Characteristics of Hgb C Carriers in Northern Israel and Clinical Features Among Hgb Homozygous
Condition: Hgb C Hemoglobinopathy
Intervention: Procedure: Medical history and basic laboratory analysis

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