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Categorize All Studies in ClinicalTrials.gov
Main Category
: Rare Diseases, Alphabetic (A-Z)
Rare Disease First Letter
: Rare Diseases Starting with M
Search for Rare Disease
Click on a link to search for the Rare Disease. Use the back button to return to this page to try another Rare Disease.
Macular Degeneration
302 studies
Malaria
350 studies
Malignant Astrocytoma
7 studies
Malignant Fibrous Histiocytoma
45 studies
Malignant Germ Cell Tumor
44 studies
Malignant Hyperthermia
1 study
Malignant Mesenchymal Tumor
604 studies
Malignant Mixed Mullerian Tumor
3 studies
Mansonelliasis
3 studies
Mantle Cell Lymphoma
638 studies
Marburg Hemorrhagic Fever
1 study
Marchiafava-Micheli Disease
23 studies
Marfan Syndrome
10 studies
Mast Cell Disease
23 studies
MAT Deficiency
1 study
McCune Albright Syndrome
11 studies
Measles
65 studies
Medulloblastoma
158 studies
Melanoma of the Choroid
55 studies
Melanoma, Familial
33 studies
MELAS Syndrome
3 studies
Membranoproliferative Glomerulonephritis (type 2)
1 study
Membranous Nephropathy, Idiopathic
15 studies
Meningocele
2 studies
Meningococcal Infection
80 studies
Meningococcemia
8 studies
Meningomyelocele
4 studies
Menkes Syndrome
2 studies
Mercury Poisoning
1 study
Merkel Cell Cancer
6 studies
Metabolic Disorder
117 studies
Metachromatic Leukodystrophy
10 studies
Metastatic Squamous Neck Cancer With Occult Primary
116 studies
Methylmalonic Acidemia
1 study
Mevalonic Aciduria
1 study
Microcephaly
2 studies
Microencephaly
2 studies
Microphthalmia
3 studies
Microscopic Polyangiitis
16 studies
Microsporidiosis
1 study
Mitochondrial Neurogastrointestinal Encephalopathy Syndrome
2 studies
Mitochondrial Trifunctional Protein Deficiency
2 studies
Mixed Connective Tissue Disease
4 studies
Miyoshi Myopathy
2 studies
Mobius Syndrome
2 studies
Mondini Dysplasia
1 study
Monoclonal Gammopathy of Undetermined Significance
59 studies
Monosomy X
34 studies
Morquio Syndrome
3 studies
Motor Neuro-ophthalmic Disorders
1 study
Motor Neuron Disease
38 studies
Motor Neuropathy
6 studies
Moyamoya Disease 1
1 study
Muckle-Wells Syndrome
5 studies
Mucopolysaccharidosis I
18 studies
Mucopolysaccharidosis Type 6
4 studies
Mucopolysaccharidosis Type II
9 studies
Muenke Syndrome
1 study
Multicentric Castlemans Disease
5 studies
Multifocal Choroiditis
2 studies
Multiple Hereditary Exostoses
3 studies
Multiple Myeloma
955 studies
Multiple Sclerosis
390 studies
Multiple System Atrophy
21 studies
Mumps
43 studies
Muscular Dystrophy
50 studies
Muscular Dystrophy, Duchenne and Becker Type
31 studies
Myalgic Encephalomyelitis
23 studies
Myasthenia Gravis
16 studies
Mycobacterium Avium Complex Infection
43 studies
Mycoplasmal Pneumonia
5 studies
Myelitis
11 studies
Myelodysplastic Myeloproliferative Disease
3 studies
Myelodysplastic Syndromes
819 studies
Myelofibrosis
256 studies
Myocarditis
6 studies
Myoclonus Epilepsy
7 studies
Myoglobinuria
1 study
Myopathy, Myotubular
1 study
Myopia, Severe
9 studies
Myositis, Inclusion Body
8 studies
Myotonia Atrophica
18 studies
Myotonia Congenita
1 study
Myotonic Dystrophy 1
18 studies
Myxoid Liposarcoma
1 study
Ménière's Disease
6 studies
Ménétrier Disease
1 study
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