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Categorize All Studies in ClinicalTrials.gov
Main Category
: Rare Diseases, Alphabetic (A-Z)
Rare Disease First Letter
: Rare Diseases Starting with A
Search for Rare Disease
Click on a link to search for the Rare Disease. Use the back button to return to this page to try another Rare Disease.
Aase Syndrome
19 studies
Abdominal Aortic Aneurysm
61 studies
Abdominal Obesity Metabolic Syndrome
97 studies
Abetalipoproteinemia
2 studies
Absent T Lymphocytes
1 study
Acanthocheilonemiasis
3 studies
Acanthocytosis
2 studies
Acanthosis Nigricans
2 studies
Achalasia
11 studies
Achondroplasia
1 study
Acoustic Neuroma
4 studies
Acquired Hemophilia
3 studies
Acromegaly
62 studies
ACTH Deficiency
1 study
Actinic Cheilitis
2 studies
Acute Articular Rheumatism
3 studies
Acute Disseminated Encephalomyelitis
2 studies
Acute Erythroblastic Leukemia
128 studies
Acute Idiopathic Polyneuritis
5 studies
Acute Intermittent Porphyria
3 studies
Acute Lymphoblastic Leukemia
788 studies
Acute Lymphoblastic Leukemia, Childhood
334 studies
Acute Monoblastic Leukemia
125 studies
Acute Mountain Sickness
13 studies
Acute Myelocytic Leukemia
999 studies
Acute Myeloid Leukemia, Adult
694 studies
Acute Myeloid Leukemia, Childhood
287 studies
Acute Myelomonocytic Leukemia
122 studies
Acute Promyelocytic Leukemia
94 studies
Acute Respiratory Distress Syndrome
118 studies
Addison's Disease
15 studies
Adenocarcinoma of Lung
141 studies
Adenoid Cystic Carcinoma
69 studies
Adenomyosis
5 studies
Adrenal Gland Hyperfunction
4 studies
Adrenal Gland Hypofunction
25 studies
Adrenal Hyperplasia
16 studies
Adrenal Incidentaloma
1 study
Adrenocortical Carcinoma
38 studies
Adult Onset Still's Disease
1 study
Advanced Sleep Phase Syndrome
1 study
Afibrinogenemia
1 study
Aggressive Fibromatosis
10 studies
Aggressive Systemic Mastocytosis
3 studies
Aicardi Syndrome
2 studies
AIDS Dementia Complex
20 studies
Alagille Syndrome
3 studies
Albers-Schonberg Disease
7 studies
Albinism
6 studies
Albright's Hereditary Osteodystrophy
4 studies
Alkaptonuria
2 studies
Allergic Bronchopulmonary Aspergillosis
5 studies
Alopecia Areata
11 studies
Alopecia Totalis
4 studies
Alopecia Universalis
2 studies
Alpha 1-antitrypsin Deficiency
23 studies
Alpha-Thalassemia
2 studies
Alport Syndrome
3 studies
Alstrom Syndrome
1 study
Alveolar Echinococcosis
1 study
Alveolar Soft Part Sarcoma
25 studies
Alzheimer Disease
534 studies
Alzheimer Disease Type 2
2 studies
Amaurosis Congenita of Leber
5 studies
Amaurosis Congenita of Leber, Type 2
1 study
Amebiasis
3 studies
Amyloid Angiopathy
1 study
Amyloid Neuropathies
3 studies
Amyotrophic Lateral Sclerosis
112 studies
Anal Cancer
59 studies
Anaplastic Large Cell Lymphoma
258 studies
Ancylostoma Duodenale
8 studies
Andersen Tawil Syndrome
2 studies
Androgenetic Alopecia
7 studies
Anemia, Hereditary Spherocytic Hemolytic
1 study
Anencephaly
4 studies
Aneuploidy
13 studies
Angelman Syndrome
5 studies
Anguillulosis
3 studies
Aniridia
8 studies
Anodontia
2 studies
Anthrax
16 studies
Antiphospholipid Syndrome
12 studies
Antisocial Personality Disorder
4 studies
Aortic Coarctation
7 studies
Aortic Valve Stenosis
46 studies
Aphthous Stomatitis
9 studies
Aplastic Anemia
96 studies
Apparent Mineralocorticoid Excess
2 studies
Apraxia
6 studies
Arachnoiditis
2 studies
Argininosuccinic Aciduria
1 study
Arima Syndrome
1 study
Arnold-Chiari Malformation
16 studies
Arrhythmogenic Right Ventricular Dysplasia
3 studies
Asbestosis
1 study
Aspartylglycosaminuria
1 study
Aspergillosis
52 studies
Asphyxia Neonatorum
10 studies
Asthenia
66 studies
Asthma
1180 studies
Astrocytoma
375 studies
Ataxia-Telangiectasia
35 studies
Atrioventricular Septal Defect
2 studies
Atypical Hemolytic Uremic Syndrome
4 studies
Atypical Mole Syndrome
2 studies
Auditory Perceptual Disorder
4 studies
Autism
146 studies
Autoimmune Enteropathy
1 study
Autoimmune Hemolytic Anemia
6 studies
Autoimmune Hepatitis
6 studies
Autoimmune Lymphoproliferative Syndrome
7 studies
Autosomal Dominant Partial Epilepsy With Auditory Features
1 study
Autosomal Dominant Polycystic Kidney Disease
22 studies
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