1 |
Acute Leukemia |
2 |
Adrenal Cancer - with distant metastases or inoperable, unresectable or recurrent |
3 |
Alexander Disease (ALX) - Neonatal and Infantile |
4 |
Amyotrophic Lateral Sclerosis (ALS) |
5 |
Anaplastic Adrenal Cancer - with distant metastases or inoperable, unresectable or recurrent |
6 |
Astrocytoma - Grade III and IV |
7 |
Bladder Cancer - with distant metastases or inoperable or unresectable |
8 |
Bone Cancer - with distant metastases or inoperable or unresectable |
9 |
Breast Cancer - with distant metastases or inoperable or unresectable |
10 |
Canavan Disease (CD) |
11 |
Cerebro Oculo Facio Skeletal (COFS) Syndrome |
12 |
Chronic Myelogenous Leukemia (CML) - Blast Phase |
13 |
Creutzfeldt-Jakob Disease (CJD) - Adult |
14 |
Ependymoblastoma (Child Brain Tumor) |
15 |
Esophageal Cancer |
16 |
Farber's Disease (FD) - Infantile |
17 |
Friedreichs Ataxia (FRDA) |
18 |
Frontotemporal Dementia (FTD), Picks Disease -Type A - Adult |
19 |
Gallbladder Cancer |
20 |
Gaucher Disease (GD) - Type 2 |
21 |
Glioblastoma Multiforme (Brain Tumor) |
22 |
Head and Neck Cancers - with distant metastasis or inoperable or uresectable |
23 |
Infantile Neuroaxonal Dystrophy (INAD) |
24 |
Inflammatory Breast Cancer (IBC) |
25 |
Kidney Cancer - inoperable or unresectable |
26 |
Krabbe Disease (KD) - Infantile |
27 |
Large Intestine Cancer - with distant metastasis or inoperable, unresectable or recurrent |
28 |
Lesch-Nyhan Syndrome (LNS) |
29 |
Liver Cancer |
30 |
Mantle Cell Lymphoma (MCL) |
31 |
Metachromatic Leukodystrophy (MLD) - Late Infantile |
32 |
Niemann-Pick Disease (NPD) - Type A |
33 |
Non-Small Cell Lung Cancer - with metastases to or beyond the hilar nodes or inoperable, unresectable or recurrent |
34 |
Ornithine Transcarbamylase (OTC) Deficiency |
35 |
Osteogenesis Imperfecta (OI) - Type II |
36 |
Ovarian Cancer - with distant metastases or inoperable or unresectable |
37 |
Pancreatic Cancer |
38 |
Peritoneal Mesothelioma |
39 |
Pleural Mesothelioma |
40 |
Pompe Disease - Infantile |
41 |
Rett (RTT) Syndrome |
42 |
Salivary Tumors |
43 |
Sandhoff Disease |
44 |
Small Cell Cancer (of the Large Intestine, Ovary, Prostate, or Uterus) |
45 |
Small Cell Lung Cancer |
46 |
Small Intestine Cancer - with distant metastases or inoperable, unresectable or recurrent |
47 |
Spinal Muscular Atrophy (SMA) - Types 0 And 1 |
48 |
Stomach Cancer - with distant metastases or inoperable, unresectable or recurrent |
49 |
Thyroid Cancer |
50 |
Ureter Cancer - with distant metastases or inoperable, unresectable or recurrent |