Mucopolysaccharidoses Publications

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Mucopolysaccharidoses Fact Sheet

Mucopolysaccharidoses information sheet compiled by the National Institute of Neurological Disorders and Stroke (NINDS).

Gene Therapy Repairs Neurological Damage in Animal Model for Rare Metabolic Disease
May 2002 news summary on gene therapy in a mouse model for Sly disease (mucopolysaccharidosis VII).

The Glycoproteinoses: An International Workshop on Advances in Pathogenesis and Therapy
The Glycoproteinoses: An International Workshop on Advances in Pathogenesis and Therapy