Gene Therapy : NIDDK

Gene Therapy

The Gene Therapy Program encompasses research aimed at developing basic and applied gene therapy for genetic metabolic diseases. Specific areas of support include:

  • Studies to improve gene delivery systems; 
  • Studies of the basic biology of AAV, adenovirus, retrovirus, and lentivirus vectors; 
  • Studies of nonviral methods of gene transfer such as liposomes or DNA conjugates;
  • Studies to target gene delivery to specific cell types;
  • Studies of gene therapy of stem cells to treat a genetic metabolic disease.

For further information, contact Dr. Catherine McKeon,  Senior Advisor for Genetic Research.

Resources for Researchers

Clinical Research


Funding for Special Communities


Funding Opportunities


Related Study Sections

See Also

Page last updated: November 25, 2008

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