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Found 57 studies with search of:   "Muscular Dystrophy"
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Rank Status Study
1 Active, not recruiting Phase 2b Study of PTC124 in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Interventions: Drug: PTC124;   Drug: PTC124;   Drug: PTC124
2 Completed Gentamicin Treatment of Muscular Dystrophy
Conditions: Becker Muscular Dystrophy;   Duchenne Muscular Dystrophy
Intervention: Drug: Gentamicin
3 Active, not recruiting The Efficacy of Using Far Infrared Radiation to Manage Muscular Dystrophies
Condition: Muscular Dystrophies
Intervention: Radiation: Far Infrared Radiation
4 Recruiting Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
Conditions: Myotonic Dystrophy;   Muscular Dystrophy, Facioscapulohumeral;   Muscular Dystrophy
Intervention:
5 Recruiting Test-Retest Reliability of Pulmonary Function Tests in Patients With Duchenne's Muscular Dystrophy
Conditions: Duchenne's Muscular Dystrophy;   Scoliosis
Intervention:
6 Completed High-Dose Prednisone in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: Prednisone
7 Recruiting Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)
Condition: Muscular Dystrophies
Interventions: Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- Lower dose;   Genetic: Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- Higher dose
8 Recruiting A Clinical Evaluation of FKRP Muscular Dystrophy
Condition: Muscular Dystrophy
Intervention:
9 Completed Safety and Efficacy Study of PTC124 in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: PTC124
10 Recruiting Ramipril Versus Carvedilol in Duchenne and Becker Patients
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Interventions: Drug: carvedilol;   Drug: ramipril
11 Active, not recruiting Safety Study of Mini-Dystrophin Gene to Treat Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Gene Transfer: rAAV vector expressing Mini-Dystrophin with CMV promoter
12 Recruiting The Preventive Efficacy of Carvedilol on Cardiac Dysfunction in Duchenne Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy;   Cardiomyopathies
Intervention: Drug: Carvedilol
13 Active, not recruiting Arrhythmias in Myotonic Muscular Dystrophy
Conditions: Muscular Dystrophy;   Arrhythmia;   Sudden Cardiac Death
Intervention: Other: Screening
14 Active, not recruiting Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: AVI-4658 (PMO)
15 Completed Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy (DMD)
Interventions: Drug: idebenone;   Drug: placebo
16 Active, not recruiting Treatment of Dysphagia in Oculopharyngeal Muscular Dystrophy by Autologous Transplantation of Myoblasts
Condition: Muscular Dystrophy, Oculopharyngeal
Intervention: Procedure: Autologous myoblasts transplantation and myotomy
17 Completed Phase III Randomized, Double-Blind Study of Prednisone for Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: prednisone
18 Recruiting Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention:
19 Completed Electrostimulation of Shoulder Girdle and Quadriceps Muscles in Facioscapulohumeral Muscular Dystrophy Patients
Condition: Facioscapulohumeral Muscular Dystrophy
Intervention: Procedure: electrostimulation
20 Completed Effect of Oral Glutamine on Muscle Mass and Function in Duchenne Muscular Dystrophy
Condition: Muscular Dystrophy, Duchenne
Interventions: Drug: L-Glutamine;   Drug: placebo

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