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Found 10 studies with search of:   Open Studies | "Beta-Thalassemia"
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Rank Status Study
1 Recruiting Evaluating the Efficacy of Deferasirox in Transfusion Dependent Chronic Anaemias (Myelodysplastic Syndrome, Beta-Thalassaemia Patients) With Chronic Iron Overload
Conditions: Myelodysplastic Syndromes;   Beta-Thalassemia
Intervention: Drug: deferasirox
2 Recruiting Evaluating the Safety of G-CSF Mobilization in Individuals With Beta Thalassemia Major
Condition: Beta-Thalassemia
Intervention: Drug: Hydroxyurea
3 Not yet recruiting Phase 2 Study of HQK-1001 in Patients With Beta Thalassemia
Condition: Beta Thalassemia
Interventions: Drug: HQK-1001;   Drug: Placebo
4 Recruiting Genetic Factors Affecting the Severity of Beta Thalassemia
Condition: Beta Thalassemia
Intervention:
5 Recruiting Assess the Feasibility and Safety of GCSF Mobilization of CD34+ Hematopoietic Progenitor Cells in Patients With Betathalassemia Major
Conditions: Beta Thalassemia Major;   Congenital Anemias
Intervention: Genetic: GCSF, Central venous line placement, Stem cell Collection (leukapheresis)
6 Recruiting Stem Cell Transplant in Sickle Cell Disease and Thalassemia
Conditions: Sickle Cell Disease;   Beta Thalassemia
Interventions: Drug: Busulfan;   Drug: Fludarabine;   Drug: Alemtuzumab;   Procedure: Allogeneic stem cell transplant
7 Recruiting Evaluating the Safety and Effectiveness of Decitabine in People With Thalassemia Intermedia
Condition: Thalassemia
Intervention: Drug: Decitabine (USAN, INN)
8 Not yet recruiting Endocrine and Nutritional Assessment in B Thalassemia Major
Condition: Thalassemia
Intervention: Procedure: Nutrition
9 Recruiting Phase II Randomized Trial of Arginine Butyrate Plus Standard Local Therapy in Patients With Refractory Sickle Cell Ulcers
Conditions: Skin Ulcers;   Sickle Cell Anemia
Intervention: Drug: arginine butyrate
10 Recruiting Allogeneic Stem Cell Transplantation Following Chemotherapy in Patients With Hemoglobinopathies
Conditions: Hemoglobinopathies;   Sickle Cell Disease;   Thalassemia
Interventions: Drug: Busulfex;   Drug: Fludarabine;   Drug: Alemtuzumab;   Procedure: Stem Cell Transfusion

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