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Found 39 studies with search of:   "Beta-Thalassemia"
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Rank Status Study
21 Completed Diagnostic Pilot Study of Dual Energy Absorptiometry in the Detection of Osteopenia or Osteoporosis in Patients With Thalassemia Major
Conditions: Osteoporosis;   Thalassemia Major;   Osteopenia
Intervention:
22 Completed 5-Azacytidine and Phenylbutyrate to Treat Severe Thalassemia
Condition: Beta Thalassemia
Intervention: Drug: 5-Azacytidine
23 Terminated Combination Therapy Compared With Single-Drug Therapy in Patients With Cardiac Diseases
Conditions: Cardiovascular Diseases;   Heart Diseases;   Beta-Thalassemia
Interventions: Drug: Deferoxamine;   Drug: Deferiprone (L1)
24 Completed Cord Blood Transplantation for Sickle Cell Anemia and Thalassemia
Conditions: Hematologic Diseases;   Anemia, Sickle Cell;   Beta-Thalassemia;   Hematopoietic Stem Cell Transplantation
Interventions: Drug: Sangstat;   Drug: Cyclophosphamide;   Drug: Busulfan;   Drug: Mycophenolate Mofetil;   Drug: Cyclosporine;   Procedure: Cord Blood Transplantation
25 Completed Chelation Therapy of Iron Overload With Pyridoxal Isonicotinoyl Hydrazone
Conditions: Anemia (Iron-Loading);   Beta-Thalassemia;   Hematologic Diseases;   Hemoglobinopathies;   Thalassemia;   Iron Overload
Intervention: Drug: chelation therapy
26 Completed Evaluation of Subcutaneous Desferrioxamine as Treatment for Transfusional Hemochromatosis
Conditions: Anemia (Iron-Loading);   Beta-Thalassemia;   Hematologic Diseases;   Hemoglobinopathies;   Thalassemia;   Iron Overload;   Hemochromatosis
Intervention: Drug: deferoxamine
27 Completed Efficacy Study in Removing Excess Iron From the Heart
Conditions: Thalassemia Major;   Hemosiderosis
Interventions: Drug: Ferriprox (deferiprone);   Drug: Desferal (deferoxamine)
28 Completed Stem Cell Transplantation (SCT) for Genetic Diseases
Conditions: Thrombocytopenia;   Metachromatic Leukodystrophy;   Fanconi's Anemia;   Thalassemia Major;   Pure Red-Cell Aplasia;   Inborn Errors of Metabolism
Intervention: Procedure: Stem Cell Transplantation
29 Completed Study of Allogeneic Bone Marrow Transplantation Using Matched, Related Donors in Patients With Nonmalignant Hematologic Disorders
Conditions: Neutropenia;   Sickle Cell Anemia;   Thalassemia Major;   Red-Cell Aplasia, Pure
Interventions: Drug: anti-thymocyte globulin;   Drug: busulfan;   Drug: cyclophosphamide;   Procedure: Bone marrow transplantation
30 Recruiting Stem Cell Transplant in Sickle Cell Disease and Thalassemia
Conditions: Sickle Cell Disease;   Beta Thalassemia
Interventions: Drug: Busulfan;   Drug: Fludarabine;   Drug: Alemtuzumab;   Procedure: Allogeneic stem cell transplant
31 Recruiting Evaluating the Safety and Effectiveness of Decitabine in People With Thalassemia Intermedia
Condition: Thalassemia
Intervention: Drug: Decitabine (USAN, INN)
32 Active, not recruiting Pilot Study for Patients With Poor Response to Deferasirox
Conditions: Transfusion-Dependent Hemachromatosis;   Thalassemia Major;   Sickle Cell Disease
Interventions: Drug: Deferoxamine;   Drug: Deferasirox;   Radiation: HIDA
33 Active, not recruiting Stem Cell Transplantation After Reduced-Dose Chemotherapy for Patients With Sickle Cell Disease or Thalassemia
Conditions: Hemoglobinopathies;   Anemia, Sickle Cell;   Hemoglobin SC Disease;   Thalassemia;   Thalassemia Major
Interventions: Drug: Busulfex;   Drug: Fludarabine;   Drug: FK506;   Drug: Prednisone
34 Not yet recruiting Endocrine and Nutritional Assessment in B Thalassemia Major
Condition: Thalassemia
Intervention: Procedure: Nutrition
35 Completed Intensive Combined Chelation Therapy for Iron-Induced Cardiac Disease in Patients With Thalassemia Major
Conditions: Iron Overload;   Cardiomyopathy
Interventions: Drug: Deferoxamine and Deferiprone;   Drug: Deferoxamine
36 Completed Examination of Protective Factors Against Severe Malaria
Conditions: Malaria;   Severe Malaria
Intervention:
37 Enrolling by invitation A Single-Arm Safety Study of Transplantation Using Umbilical Cord Blood and Human Placental-Derived Stem Cells From Partially Matched Related Donors in Persons With Certain Malignant Blood Diseases and Non-Malignant Disorders
Condition: Hematologic Malignancies
Intervention: Procedure: UCB and HPDSC
38 Recruiting Phase II Randomized Trial of Arginine Butyrate Plus Standard Local Therapy in Patients With Refractory Sickle Cell Ulcers
Conditions: Skin Ulcers;   Sickle Cell Anemia
Intervention: Drug: arginine butyrate
39 Recruiting Allogeneic Stem Cell Transplantation Following Chemotherapy in Patients With Hemoglobinopathies
Conditions: Hemoglobinopathies;   Sickle Cell Disease;   Thalassemia
Interventions: Drug: Busulfex;   Drug: Fludarabine;   Drug: Alemtuzumab;   Procedure: Stem Cell Transfusion

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