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Found 96 studies with search of: | "Sphingolipidoses" |
Rank | Status | Study | ||||
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1 | Recruiting |
Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism
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2 | Active, not recruiting |
Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation
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3 | Completed |
Study to Evaluate Blood Cell Lines From Patients With Gaucher Disease
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4 | Completed |
Stem Cell Transplantation (SCT) for Genetic Diseases
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5 | Recruiting |
Phase II Randomized Study of Alendronate Sodium for Osteopenia in Patients With Gaucher's Disease
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6 | Recruiting |
Phase II Study of Glucocerebrosidase in Patients With Gaucher Disease
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7 | Completed |
Phase I Study of Retrovirally Mediated Transfer of the Human Glucocerebrosidase Gene Into Peripheral Blood Stem Cells for Autologous Transplantation in Patients With Type I Gaucher Disease
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8 | Completed |
A Study of AT1001 in Patients With Fabry Disease
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9 | Completed |
Stem Cell Transplant for Inborn Errors of Metabolism
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10 | Recruiting |
Canadian Fabry Disease Initiative (CFDI) Enzyme Replacement Therapy (ERT) Study
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11 | Completed |
Alpha-Galactosidase A Replacement Therapy for Fabry Disease
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12 | Completed |
Dosing Study of Replagal in Patients With Fabry Disease
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13 | Recruiting |
A Study of the Effects of Fabrazyme on Mother's Lactation and on the Growth, Development and Immunologic Response of Their Infants
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14 | Completed |
PEG-Glucocerebrosidase for the Treatment of Gaucher Disease
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15 | Completed |
PET Scans in Normal Volunteers and Patients With Fabry Disease
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16 | Enrolling by invitation |
Compassionate Use of Metazym in Patients With Late Infantile Metachromatic Leukodystrophy
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17 | Completed |
Study to Collect Data on Fabry Disease Patients With Enhanceable Alpha-Galactosidase A Activity
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18 | Completed |
A 12-Week Safety and Pharmacodynamic Study of AT1001 in Female Patients With Fabry Disease
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19 | Recruiting |
Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
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20 | Recruiting |
Genetic Studies of Lysosomal Storage Disorders
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