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Found 31 studies with search of:   "Mucopolysaccharidoses"
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Rank Status Study
1 Active, not recruiting Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation
Conditions: I Cell Disease;   Fucosidosis;   Globoid Cell Leukodystrophy;   Adrenoleukodystrophy;   Mannosidosis;   Niemann-Pick Disease;   Pulmonary Complications;   Mucopolysaccharidosis I;   Mucopolysaccharidosis VI;   Metachromatic Leukodystrophy;   Gaucher's Disease;   Wolman Disease
Intervention:
2 Recruiting Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis (MPS) I
Conditions: Mucopolysaccharidosis I;   Lysosomal Storage Diseases;   Spinal Cord Compression
Intervention: Drug: laronidase
3 Completed Stem Cell Transplantation for Hurler
Conditions: Mucopolysaccharidosis I;   Mucopolysaccharidosis VI;   Mannosidosis;   Mucolipidosis Type II (I-Cell Disease)
Interventions: Procedure: Stem Cell Transplant;   Drug: Busulfan, Cyclophosphamide, ATG
4 Completed Study of rhASB in Patients With Mucopolysaccharidosis VI
Condition: Mucopolysaccharidosis VI
Intervention: Drug: N-acetylgalactosamine 4-sulfatase
5 Completed Study of Aldurazyme® Replacement Therapy in Patients With Mucopolysaccharidosis I (MPS I) Disease
Condition: Mucopolysaccharidosis I
Intervention: Drug: Recombinant Human Alpha-L-Iduronidase, Aldurazyme® (laronidase)
6 Completed A Dose-Optimization Study of Aldurazyme® (Laronidase) in Patients With Mucopolysaccharidosis I (MPS I) Disease
Conditions: Mucopolysaccharidosis I;   Hurler's Syndrome;   Hurler-Scheie Syndrome;   Scheie Syndrome
Intervention: Drug: Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
7 Completed Phase 3 Extension Study of the Safety and Efficacy of Aldurazyme® (Laronidase) in Mucopolysaccharidosis I (MPS I) Patients
Conditions: Mucopolysaccharidosis I;   Hurler's Syndrome;   Hurler-Scheie Syndrome;   Scheie Syndrome
Intervention: Drug: Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
8 Recruiting A Study of the Effect of Aldurazyme® (Laronidase) Treatment on Lactation in Female Patients With Mucopolysaccharidosis I (MPS I) and Their Breastfed Infants
Conditions: Mucopolysaccharidosis I;   Hurler's Syndrome;   Hurler-Schei Syndrome;   Scheie Syndrome
Intervention: Drug: Aldurazyme (laronidase)
9 Completed Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome)
Condition: Mucopolysaccharidosis II
Intervention: Gene Transfer: lymphocyte gene therapy
10 Completed Iduronate-2-Sulfatase Enzyme Replacement Therapy in Mucopolysaccharidosis II (MPS II)
Condition: Mucopolysaccharidosis II
Intervention: Drug: Iduronate-2-sulfatase enzyme replacement therapy
11 Recruiting Extension Study of Intrathecal Enzyme Replacement Therapy for MPS I
Conditions: Spinal Cord Compression;   Mucopolysaccharidosis I;   Hurler-Scheie Syndrome;   Scheie Syndrome;   Lysosomal Storage Disease
Intervention: Drug: laronidase
12 Recruiting Immune Tolerance Study With Aldurazyme®
Condition: Mucopolysaccharidosis I
Interventions: Biological: Aldurazyme® (laronidase);   Drug: Neoral® (CsA);   Drug: Imuran® (Aza)
13 Recruiting Mucopolysaccharidosis I (MPS I) Registry
Condition: Mucopolysaccharidosis I
Intervention:
14 Recruiting A Study Investigating the Relationship Between the Development of Laronidase Antibody and Urinary GAG Levels in Aldurazyme® Treated Patients
Conditions: Mucopolysaccharidosis I;   Hurler's Syndrome;   Hurler-Scheie Syndrome;   Scheie's Syndrome
Intervention: Drug: Aldurazyme® (laronidase)
15 Completed A Study Evaluating the Safety and Pharmacokinetics of Aldurazyme® (Laronidase) in MPS I Patients Less Than 5 Years Old
Conditions: Confirmed Diagnosis of Mucopolysaccharidosis I;   Less Than 5 Years of Age
Intervention: Drug: Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
16 Recruiting A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
Condition: MPS IV A
Intervention:
17 Recruiting A Phase 4 Two Dose Level Study of Naglazyme(TM) (Galsulfase) in Infants With MPS VI
Conditions: Mucopolysaccharidosis VI;   Maroteaux-Lamy Syndrome
Intervention: Drug: galsulfase
18 Completed Open-Label Study of Efficacy and Safety of Recombinant Human N-Acetylgalactosamine 4-Sulfatase in Patients With MPS VI
Condition: Mucopolysaccharidosis VI
Intervention: Drug: N-acetylgalactosamine 4-sulfatase
19 Completed Study of Recombinant Human N-Acetylgalactosamine 4-Sulfatase in Patients With MPS VI
Condition: Mucopolysaccharidosis VI
Intervention: Drug: N-acetylgalactosamine 4-sulfatase
20 Completed Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II Patients Receiving Idursulfase
Conditions: Hunter Syndrome;   Mucopolysaccharidosis II
Intervention: Biological: Idursulfase

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