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Found 8 studies with search of: | "Gangliosidoses" |
Rank | Status | Study | ||||
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1 | Active, not recruiting |
Pharmacokinetics and Tolerability of Zavesca® (Miglustat) In Patients With Juvenile GM2 Gangliosidosis
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2 | Completed |
Pharmacokinetics, Safety and Tolerability of Zavesca (Miglustat) in Patients With Infantile Onset Gangliosidosis: Single and Steady State Oral Doses
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3 | Recruiting |
HSCT for High Risk Inherited Inborn Errors
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4 | Completed |
Stem Cell Transplant for Inborn Errors of Metabolism
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5 | Recruiting |
Nervous System Degeneration in Glycosphingolipid Storage Disorders
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6 | Suspended |
A Phase I Study of Pyrimethamine in Patients With GM-2 Gangliosidosis
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7 | Completed |
Diagnostic and Screening Study of Genetic Disorders
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8 | Recruiting |
A Natural History Study of Hexosaminidase Deficiency in Infantile Tay-Sachs Disease
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